ARM's Clinical & Patient Education Inherited Blood Disorder Roundtable

Welcome & Introductory Remarks

Kimberly Haugstad, President & CEO, Hemophilia Federation of America
Michael Werner, Executive Director, Alliance for Regenerative Medicine

Featured Talk: Gene Therapy 101 & Clinical Outlook

Steven Pipe, M.D., Director, Division of Pediatric Hematology & Oncology; Pediatric Medical Director, Hemophilia & Coagulation Disorders Program, University of Michigan

Roundtable Discussion: State of Gene Therapy for Inherited Blood Disorders

Craig Butler, National Executive Director, Cooley’s Anemia Foundation
Sudha Parasuraman, M.D., VP of Global Medical Affairs, uniQure
Didier Rouy, M.D., Ph.D., Senior Medical Officer, Hemophilia, Sangamo BioSciences
Katie Verb, Director, Policy & Government Relations, Hemophilia Federation of America

Roundtable Discussion: Clinical Trial Recruitment & Interaction with the Patient Community

John Chapin, M.D., Medical Director, Clinical Research & Development – Hematology, Shire
Jennifer Helfer, Ph.D., Patient Advocacy, bluebird bio
Daniel Leonard, Director of Global Patient Advocacy, uniQure
Steven Pipe, M.D., Director, Division of Pediatric Hematology & Oncology; Pediatric Medical Director, Hemophilia & Coagulation Disorders Program, University of Michigan
Michelle Rice, Senior Vice President, Public Policy & Stakeholder Relations, National Hemophilia Foundation

Featured Talk: The Patient’s Perspective

John Vieke, Patient Advocate

Closing Remarks: Next Steps

Val Bias, CEO, National Hemophilia Foundation
Morrie Ruffin, Managing Director, Alliance for Regenerative Medicine

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